Unlocking Meningioma's Secrets: The Quest for New Treatments

For thousands of patients with recurring meningioma, a scientific breakthrough offers new hope where traditional treatments have reached their limits.

Imagine being diagnosed with a brain tumor that has returned after surgery and radiation, only to be told there are no standard treatments left to try. This is the reality for countless patients with recurrent meningioma, the most common primary brain tumor.

While often benign, these tumors can become aggressive, and when they return after initial treatment, options become severely limited. But across research laboratories worldwide, a revolution is underway. Scientists are peering deeper into meningioma's molecular blueprint than ever before, identifying precise targets for revolutionary new therapies that could finally change this outlook.

Why Meningioma Research Matters

41.7%

of all central nervous system tumors are meningiomas 4

10.15

people per 100,000 are affected by meningiomas 4

26-29%

six-month progression-free survival for recurrent higher-grade meningiomas 4

Meningioma WHO Grade Distribution and Recurrence Rates

The incidence of these tumors is actually on the rise, making the search for effective treatments more urgent than ever 4 .

For patients with recurrent higher-grade meningiomas, the prognosis remains challenging. The six-month progression-free survival rate is only 26-29%, highlighting the critical need for more effective systemic therapies 4 .

The New Frontier: Targeting Meningioma's Molecular Weaknesses

Traditional treatments like surgery and radiation therapy are local solutions. For tumors that recur or are inoperable, scientists are now focusing on targeted therapies that attack specific molecules that drive tumor growth.

SSTR2 Breakthrough

One of the most promising discoveries is that 80-95% of meningiomas overexpress a protein called somatostatin receptor type 2 (SSTR2) 2 4 . This receptor acts like a "flag" on the tumor's surface, providing a perfect target for precision medicine.

This finding has paved the way for theranostics - an innovative approach that combines therapy and diagnostics. Doctors can now use SSTR2-targeting PET scans to precisely locate tumors, then deliver targeted radiation directly to the cancer cells using drugs like [177Lu]Lu-DOTATATE 4 .

Emerging Molecular Targets

Beyond SSTR2, recent research has identified additional potential targets. A 2025 study that integrated genomic and proteomic data revealed several promising candidates, including BET1L, AKR1C3, and RSPO3 7 .

These molecules play key roles in tumor growth and survival pathways, offering new avenues for drug development.

Target Expression Levels:
SSTR2 95%
BET1L 65%
AKR1C3 58%
RSPO3 42%

A Closer Look: The ANXA3 Discovery

In 2025, researchers at the University of Plymouth's Brain Tumour Research Centre of Excellence published a groundbreaking study in the journal eBioMedicine that could transform how we treat certain meningiomas 8 .

The Methodology: Step by Step

The research team, led by Professor Oliver Hanemann, followed a systematic approach:

Analysis of Tumor Biology

They began by studying the molecular drivers of meningioma growth, particularly focusing on tumors linked to mutations in the NF2 gene, the most common genetic cause of meningioma.

Identification of ANXA3

Through their investigation, they identified a specific protein called ANXA3 that appears to drive the growth of certain meningioma cells.

Laboratory Experiments

Researchers then conducted experiments in which they blocked the ANXA3 protein in meningioma cell cultures and observed the effects on tumor growth.

Results and Analysis

The findings were significant. By blocking ANXA3 in laboratory settings, researchers were able to slow—and in some cases completely stop—meningioma cell growth 8 .

This discovery is particularly important for patients whose meningiomas are driven by NF2 gene mutations, as these tumors may be especially reliant on the ANXA3 protein for their growth and survival. Professor Hanemann explained: "Targeting ANXA3 may offer a more personalized approach to treating meningiomas in future, particularly for patients whose meningioma is a result of a mutation in the NF2 gene" 8 .

ANXA3 Discovery: Key Findings and Potential Impact

From Bench to Bedside: Clinical Trials Bringing Hope to Patients

Laboratory discoveries are meaningless unless they can be translated into treatments for patients. Fortunately, several clinical trials are now testing these new approaches.

The LUMEN-1 Trial: A Major Step Forward

In March 2025, the European Organisation for Research and Treatment of Cancer (EORTC) launched the LUMEN-1 clinical trial, a groundbreaking study investigating [177Lu]Lu-DOTATATE for recurrent meningioma 1 2 .

Trial Details
  • Official Name EORTC-2334-BTG
  • Study Phase Phase II
  • Patient Population 136 patients
  • Estimated Completion 2029
Trial Design

The trial's primary goal is to determine whether the targeted treatment can improve progression-free survival - the length of time patients live without their disease worsening. Secondary objectives include assessing overall survival, safety, quality of life, and neurological function 1 2 .

Other Promising Approaches

Beyond radiation-based therapies, researchers are exploring multiple angles to combat meningioma:

Gene Therapy

Approaches using small interfering RNAs (siRNAs) and microRNAs (miRNAs) show potential for selectively silencing oncogenic drivers in meningioma .

Nanomedicine

The application of nanotechnology could significantly improve the delivery of gene therapies, though research in this area for meningioma is still in early stages .

Drug Combinations

The CEVOREM trial investigated combination therapies, achieving a six-month progression-free survival rate of 55% 4 .

The Scientist's Toolkit: Essential Resources for Meningioma Research

What does it take to conduct this cutting-edge meningioma research? Here are some of the key tools and reagents scientists are using to advance the field:

SSTR2 PET Imaging

Detects somatostatin receptor-positive tumors for diagnosis and patient selection for targeted therapy 4 6 .

Diagnostic
ANXA3 Inhibitors

Experimental compounds that block the ANXA3 protein to slow tumor growth in NF2-mutant meningioma 8 .

Therapeutic
siRNAs and miRNAs

Small nucleic acid molecules that can silence specific oncogenic drivers; potential for gene therapy approaches .

Gene Therapy
Nanoparticle Delivery Systems

Enhances the stability and targeted delivery of gene therapies across the blood-brain barrier .

Delivery

The Future of Meningioma Treatment

The landscape of meningioma treatment is evolving from a one-size-fits-all approach to personalized precision medicine. As Dr. Karen Noble of Brain Tumour Research noted: "This breakthrough is a powerful example of the progress we can make with sustained investment in research. It offers real promise for transforming how we treat meningiomas and gives fresh hope to thousands of patients" 8 .

Evolution of Meningioma Treatment Approaches

"Greater awareness and less invasive treatment options can't come soon enough. If future patients can be spared the kind of surgery I went through and the life-changing effects that followed, then this research brings hope — not just for treatment, but for better outcomes and quality of life."

Esme Morris, meningioma patient

The integration of molecular diagnostics with advanced imaging and targeted therapies will likely define the next chapter in meningioma care. Patients who once faced limited options may soon have treatments tailored to their tumor's specific genetic profile and molecular characteristics.

As research continues to unravel the complexity of meningioma, the hope is that what today seems like experimental science will become tomorrow's standard of care, offering new options for patients facing this challenging diagnosis.

References